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Dernières publications
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Valentina Taglietti, Kaouthar Kefi, Lea Rivera, Oriane Bergiers, Nastasia Cardone, et al.. Thyroid-stimulating hormone receptor signaling restores skeletal muscle stem cell regeneration in rats with muscular dystrophy. Science Translational Medicine, 2023, 15 (685), ⟨10.1126/scitranslmed.add5275⟩. ⟨hal-04150315⟩
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A. Morin, Amalia Stantzou, Olga N. Petrova, John C.W. Hildyard, T. Tensorer, et al.. Dystrophin myonuclear domain restoration governs treatment efficacy in dystrophic muscle. Proceedings of the National Academy of Sciences of the United States of America, 2023, 120 (2), ⟨10.1073/pnas.2206324120⟩. ⟨hal-04122777⟩
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Valentina Taglietti, Kaouthar Kefi, Iwona Bronisz-Budzyńska, Busra Mirciloglu, Mathilde Rodrigues, et al.. Duchenne muscular dystrophy trajectory in R-DMDdel52 preclinical rat model identifies COMP as biomarker of fibrosis. Acta Neuropathologica Communications, 2022, 10 (1), ⟨10.1186/s40478-022-01355-2⟩. ⟨hal-03828280⟩
Chiffres clés
48
Publications avec texte intégral
Open Access
67 %
Mots clés
LncRNA
Dystrophie musculaire de Becker
Exon skipping
Dystrophy
Duchenne muscular dystrophy
Myogenesis
NNOS
Muscular Dystrophy
Mdx mouse
Cells
Allele‐specific silencing therapy
Skeletal muscle
Cardiomyopathie
Dynamin 2
Centronuclear myopathy
Energy Metabolism/drug effects
Inbred mdx
L-Type
Immunoglobulin Fc Fragments/pharmacology
Dystrophie Musculaire de Duchenne DMD
Diseases
Multi exon skipping
Muscular dystrophy
Antisense oligonucleotides
Male
Cultured
Muscles/physiopathology
LKB1
MiARN
DMO
Inbred C57BL
Dystrophie Musculaire de Becker BMD
Génomique
Becker BMD muscular dystrophy
Cell Biology
Human Umbilical Vein Endothelial Cells
Modificateurs de gènes
Invivo
Gene Expression Regulation/drug effects
Liver
CD38
Mice
Autophagy
Metabolism
Calcium Channels
NAD+
Animals
Delivery
Mitochondrial fission
Muscle development
Dystrophin-EGFP
Knockout
Gene expression
Base Sequence
Cachexia
Cell Line
Myotendinous junction
Muscle Biology
DMD
Morphogenesis
Homeostasis
Activin Receptors
Molecular docking
Long QT
Becker muscular dystrophy
BMD
Duchenne DMD dystrophy
Muscle
Gene modifiers
Duchenne muscular dystrophy DMD
Clinical trials
Epigenetics
CaVβs
Genomic
Becker muscular dystrophy BMD Duchenne muscular dystrophy DMD miRNA nNOS
DHPR α1S
Muscular Atrophy
Calcium
Multiresolution modeling
Animal/physiopathology
Multi resolution modeling
Muscle Strength
MES
Drp1
CaV subunits
Ex-vivo
Inhibitors
Cardiomyopathy
Cell homeostasis
Molecular Sequence Data
LncARN
CTNNB1
Long noncoding RNA
Hear
Hepatocellular carcinoma
Dystrophin central domain
Humans
Dystrophin
Becker muscular dystrophy BMD
Dystrophine